Patients are at the center of all we do. Beginning with research and development of our medicines and continuing beyond approval, we partner with patient communities to understand their specific priorities and develop ways to provide support, including:

• Access to our medicines through our Expanded Access Policy
• Patient support programs that drive product education and disease awareness, such as grocery store tours exploring low-Phe food options for those with PKU
• Grants for a variety of events, activities and projects that educate patients and increase awareness about complex conditions
• Support for Investigator Initiated Studies to advance scientific innovation for complex conditions
• Additional support programs such as RARE Scholars, an annual scholarship for students living with rare conditions

Access to Our Therapies in Low- and Middle-Income Regions

As part of our commitment to expanding access to our medicines, we work to ensure that people from low- and middle-income regions have access to our medicines. Treatment for rare conditions comes with unique challenges, and the path to access varies in each region. For these reasons, we partner with all those involved in breaking down regional obstacles and facilitating paths to care, including doctors, health officials, researchers, community advocates, suppliers and patients themselves. Our approach includes:

• Reaching national pricing agreements in a number of low- and middle-income countries
• Adjusting established agreements following major regional events such as armed conflict and natural disasters
• Tailoring drug delivery processes to meet unique regional needs: for example, identifying ways to maintain frozen medicines in route to areas with infrastructure challenges
• Partnering in initiatives to improve diagnostic capacity and identify those in need of treatment
• Designing patient support programs that address specific barriers to care in individual regions

Learn more about how we support patient communities

We take on some of the toughest challenges in science and medicine to transform care for people with serious medical conditions. To succeed in this mission, we rely on a diverse community of employees who feel empowered and safe to bring all perspectives and ideas to the table. Our efforts to advance diversity, equity and inclusion (DEI) include:

• Promoting DEI by understanding, supporting and celebrating differences in race, ethnicity, gender, age, religion, disability and sexual orientation across the organization and beyond
• Adhering to a Global Code of Conduct and Business Ethics to conduct all aspects of our business in accordance with the highest standards of ethical behavior
• Providing an open-door policy and EthicsPoint hotline that allow employees to ask questions or submit potential policy violations
• Participating in the Western Regional Minority Supplier Development Council (WRMSDC) – providing access to certified minority suppliers, supplier diversity program development and more

Learn more about our commitment to diversity, equity and inclusion

Supporting the communities where we live and work is central to who we are. We provide funding and support for a variety of activities, projects and events focused on patients, the scientific and medical communities, and public health initiatives in areas of interest to 澳门正规博彩十大排行平台.

With our passion for science, we also focus our philanthropic giving on educational programs that encourage scientific training among the underserved and developing the next generation.

Learn more about how we support our communities through corporate giving initiatives